Vertex’s gene therapy shows promise in younger children with blood disorders

Vertex’s gene therapy shows promise in younger children with blood disorders

The Straits Times - Sports·2025-12-06 21:03

Vertex Pharmaceuticals said on Dec 6 that its gene therapy helped children aged between 5 and 11 with sickle cell disease (SCD) to be free of painful events.

The therapy also allowed those with another blood disorder that requires frequent blood transfusions to be transfusion-free for at least 12 consecutive months.

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